Gene Therapy for Disease Treatment

Gene therapy is a treatment approach that changes gene activity to help address disease. It focuses on the genetic cause of a problem rather than only easing symptoms. In this way, it is used in disease intervention.

One common strategy is to replace a faulty gene with a normal copy. Another stra...

Gene therapy is the insertion of a gene into an individual's cells to prevent or treat serious diseases. The inserted gene may be a healthy copy of a mutated gene, or it may be a different gene that counteracts the effects of a faulty gene.

Genes can be delivered in vivo, directly into a person, or ex vivo, into cells removed from the bo...