Gene Therapy for Disease Treatment

Gene therapy is a treatment approach that changes gene activity to help address disease. It focuses on the genetic cause of a problem rather than only easing symptoms. In this way, it is used in disease intervention.

One common strategy is to replace a faulty gene with a normal copy. Another stra...

Gene therapy is the introduction of a gene into a patient’s cells to treat or prevent a disease caused by a mutated gene.

The introduced gene may be a functional copy of the mutated gene, or it may be a different gene that helps counter the effects of the mutation.

The therapeutic gene can be delivered directly into the patient’s bod...